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Mychal-Anne, 3-MCC
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Denoires
Propionic Acidemia
9/20/2001 - 4/25/2005
Home
About Us
>
Board of Directors
Medical Advisors
>
Kimberly A. Chapman
Carla Cuthbert
Elaina Jurecki
Dr. Stephen Kahler
Mark Korson
Piero Rinaldo
Mendel Tuchman
Keiko Ueda
Charles Venditti MD
Jerry Vockley MD PhD
Metabolic Diet APP
What We Know About Ammonia In Organic Acidemias
Contact Us/Facebook Group
OA Disorders
MHBD
2MBCD
3-Hydroxyisobutyric Acidemia
3-MCC
5-oxoprolinemia
BKT
CMAMMA
Cobalmin X
D2-HGA
GA-I
HMG
ICBD
IVA
>
IVA Questionnaire Survey
L2HGA
MA
MCD
MGA
MMA
>
Sources of Hydroxycobalamin
Major Milestone in MMA Research
Quality of Life MMA Survey
PA
>
PA Twins - Rare
PA Study at the NIH
Fishing for New Drugs for Propionic Acidemia
PA Articles
PA Nutritional Guidelines
PA Research Update
Liver Transplantation for Propionic and Methylmalonic Acidemias
Effective Gene Therapy for Propionic Acidemia in Mice
PA Consensus Conference Articles
HIBCH
OAA Patient Registry
TedTalk-Saving a Child with a Rare Disease
New Drug Relieves TCA Cycle Block In Patients With PA And MMA
Autism & Metabolism
OAA Research Fund
Novel Gene Medicine Approach for Treatment of Rare Early Onset Diseases
Gene Therapy Update
PA Study at the NIH
Novel Messenger RNA Therapeutic Approach
HemoShear Therapeutics Making Progress Toward Potential Treatment for OA Diseases
Services
OAA Brochure
OAA Newsletter
Newsletter Archive
Nutrition & Recipies
>
Fiber Article
Low Protein
Metabolic Formula Suppliers
Metabolic Clinics/Testing Facilities
Insurance Information
>
Health insurance coverage for OAA
OAA Google Group/Facebook
OAA Inspire Forum
Page Translator
Questionnaire
Support Us
Fundraising for OAA
Membership Donation
Donate
OAA Research Donations
Volunteer
Events
2018 FOD/OAA National Metabolic Conference
2017 OAA Graduates
2016 OAA Conference Video
2016 Conference Presentations
2016 Conference Sponsors
2016 FOD/OAA National Metabolic Family Conference
2012 FOD/OAA National Metabolic Family Conference
2014 Conference Sponsors
2014 FOD/OAA National Metabolic Family Conference
Newborn Screening
Links
Informational Websites
Nutrition Links
Education Resources
Welcome to Holland
Memorials
Our Kids
Amber, Age 33
Annabelle PA
Bryan, PA
Connor & Nathan, D2-HGA
Elizabeth, PA
Grant and Sebastian, PA
Malik, IVA
Michael, MMA Cbl C
Molly, 3MCC
Mychal-Anne, 3-MCC
Olivia, IVA, Age 24
Shane, Kaden, Kyler Cbl F
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